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Rostudirsen

杜氏肌营养不良

Rostudirsen is a phosphorodiamidate morpholino oligomer designed to target Duchenne muscular dystrophy (DMD) by promoting exon skipping in muscle cells. It functions through the selective delivery of therapeutic oligonucleotides to skeletal muscle, facilitating the production of internally shortened dystrophin protein, which is crucial for muscle integrity and function. This reagent is instrumental in advancing research on DMD gene therapies and evaluating the efficacy of treatments aimed at restoring dystrophin expression in affected tissues.

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Specifications

Manufacturer	Adooq Bioscience
CAS Number	3028750-59-3
Applications	杜氏肌营养不良
Molecular Weight	10451.91
Synonyms	DYNE-251 Oligomer

Storage & Solubility

In Vitro Solubility

Reported Solubility

No reported solubility data are available for this product.

Preparing Stock Solutions

Stock preparation is unavailable for this product molecular weight.

Calculated stock concentrations do not establish solvent solubility. Refer to the reported solubility data for experimental guidance.

Storage

Store powder at -20°C, keep desiccated.
In powder form, the chemical is stable for 36 months.
In solution, store at -20°C and use within 1 month to prevent loss of potency. Aliquot to avoid multiple freeze/thaw cycles.